Exa-cel, a new CRISPR-based treatment, modifies the genes of the patient's stem cells to induce them to produce fetal hemoglobin. I have a long-standing interest in sickle cell anemia, a genetic ...

A class of drugs used for their ability to stop tumor cells from dividing is now under study for their potential to reduce the pain and damage caused by sickle cell disease, investigators report. The ...

Learn how gene editing is transforming sickle cell disease treatment and why expanding access to younger children matters.

Researchers from multiple institutions in China have found a way to use gene editing to reactivate dormant fetal oxygen-transporting proteins in adult blood cells to potentially reverse a wide range ...

Gene editing has delivered remarkable results against sickle cell disease. Now researchers are working to make these ...

People with sickle cell anemia, especially children, are more likely to experience a stroke. Silent strokes, which don’t cause noticeable symptoms, are especially common. Sickle cell anemia (SCA) is a ...

The first person to ever be cured of sickle cell anemia in Louisiana received revolutionary gene therapy. The treatment is ...

Within 12 hours of landing in Florida in January, 2021, Sebastien Beauzile, then 17, was admitted to two separate hospitals. He had come to Florida to surprise his sister for her birthday. But instead ...

He's the first in New York to receive the novel treatment and one of the first in the world. Share on Facebook (opens in a new window) Share on X (opens in a new window) Share on Reddit (opens in a ...

Share on Pinterest There may soon be a new treatment for sickle cell anemia that uses gene-editing techniques that could potentially cure the disease. SDI Productions/Getty Images For the first time, ...